Hepatotoxicity in AAV Gene Therapy: Clinical Challenges and Strategic Solutions
https://www.jpeds.com/article/S0022-3476(26)00345-8/fulltext?rss=yes
The Journal of Pediatrics
Hepatotoxicity in AAV Gene Therapy: Clinical Challenges and Strategic Solutions
The most common adverse event after administration of AAV gene therapy has been varying
degrees of hepatotoxicity.1 The clinical presentation is predominantly characterized
by asymptomatic elevations in serum alanine aminotransferase (ALT), aspartate aminotransferase…
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